Researchers discovered that suppressing BMP signaling in astrocytes reduces seizures and restores brain balance in Fragile X syndrome models.

Fragile X syndrome (FXS) is an inherited genetic developmental condition that strongly impacts brain development. Despite the ...

In September last year, we reported Servier had advanced its emerging neurology pipeline into the clinical trials stage by ...

Spinogenix, Inc., a clinical-stage biopharmaceutical company pioneering first-in-class therapeutics designed to restore synapses to improve the lives of patients, is initiating CLARITY, a Phase 2b/3 ...

Fragile X syndrome (FXS) is an inherited genetic developmental condition that strongly impacts brain development. Despite ...

Collaboration with UMass Chan Medical School confirmed FMR1-217 as well as an RNA-targeted mechanism to restore functional FMRP protein to develop potential treatments for FXS QurAlis’ preliminary ...

In the Phase IIa study, 10 adult male patients with FXS received one oral dose of SPG601.

SPG601 is a first-in-class, BK-modulator with the potential to improve cognitive, emotional and sensory symptoms in FXS patients FRAXA's early preclinical support helped establish the ...

Fragile X syndrome, the most common form of inherited intellectual disability, may be unfolding in brain cells even before birth, despite typically going undiagnosed until age 3 or later. A new study ...

PLYMOUTH MEETING, Pa.--(BUSINESS WIRE)--Harmony Biosciences Holdings, Inc. (Nasdaq: HRMY), today announced topline results from its Phase 3 registrational clinical trial (the RECONNECT Study) of ...

Friday is National Fragile X Syndrome Awareness Day. Here are a few facts about this interesting syndrome and the individuals it affects: — FXS is a genetic disorder in which there is missing or ...

Add Yahoo as a preferred source to see more of our stories on Google. The drug is set to be investigated in registrational trials. Credit: bangoland / Shutterstock.com (bangoland / Shutterstock.com) ...